Metal Metabolism, Inborn Errors - 25 Studies Found Not yet recruiting : Health Burden of Hypophosphatasia : Hypophosphatasia : 2016-04-01 : Other: no intervention Completed : Post-approval Clinical Study of Asfotase Alfa Treatment for Patients With Hypophosphatasia (HPP) in Japan : Hypophosphatasia : 2015-08-11 : Biological: Asfotase Alfa Other Name: Strensiq Approved for marketing : Expanded Access Program for Asfotase Alfa Treatment for Patients With Infantile- or Juvenile-onset Hypophosphatasia (HPP) : Hypophosphatasia : 2015-07-08 : Biological: asfotase alfa Patients participating in this program will receive 6 mg/kg/week asfotase alfa Completed : Safety and Efficacy of Asfotase Alfa in Patients With Hypophosphatasia (HPP) : Hypophosphatasia : 2015-03-26 : Drug: Asfotase Alfa (ALXN1215) Other Name: ALXN1215 Enrolling by invitation : An Observational, Longitudinal, Prospective, Long-Term Registry Of Patients With Hypophosphatasia (HPP) : Hypophosphatasia (HPP) : 2014-11-26 Completed : Burden of Disease in Hypophosphatasia (HPP) : Hypophosphatasia : 2014-11-11 Recruiting : Natural History Study of Patients With Hypophosphatasia (HPP) : Hypophosphatasia : 2014-09-09 Completed : Retrospective, Non-interventional Natural History of Patients With Juvenile-onset Hypophosphatasia (HPP) : Hypophosphatasia (HPP) : 2014-03-25 Completed : A Retrospective Study of the Natural History of Patients With Severe Perinatal and Infantile Hypophosphatasia (HPP) : Hypophosphatasia (HPP) : 2011-08-16 Completed : Dose Escalation Study to Evaluate the Safety and Tolerability of Multiple Infusions of BPS804 in Adults With Hypophosphatasia (HPP) : Hypophosphatasia : 2011-07-29 : Drug: BPS804 <<< Previous | Next >>>